You can access any of the podium or poster presentations’ abstracts by searching for it below. For the 2026 FIP world congress in Montreal, presentations and summaries from invited speakers are available below, while abstracts are published in the Pharmacy Education Journal (PEJ) here.
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Personalised genetic medicines for inherited disorders
- In: SYMPOSIUM: GENE-BASED THERAPEUTICS: POSSIBILITIES AND CHALLENGES on Monday, 14 April 2014, 13:00-14:30
- At: PSWC, Melbourne (Australia) (2014)
- Type: Presentation
- By: WILTON, Steve (Murdoch University, Centre for Comparative Genomics, Perth, Australia)
- Abstract:
Background. Antisense oligonucleotides can redirect the pre-mRNA processing of targeted gene transcripts. Therapeutic alternative splicing can be employed excise a selected exon or enhance recognition of an exon normally excluded from the mature mRNA.
Aims. Duchenne muscular dystrophy (DMD), the most common and serious form of childhood muscle.. The access to the whole abstract and if available the presentation file is available to FIP members and to congress participants of that specific congress.
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Last update 23 September 2026